Langerhans cell histiocytosis: Behind the Mystery
Langerhans cell histiocytosis (LCH) is an uncommon condition that causes tissue damage and lesions in one or more parts...
Rare disease advances: FDA approves three new treatments
Keywords: rare disease, rare disorders, achondroplastic dwarfism Meta Description: In November and December 2021, the FDA approved innovative treatments...
Real-world evidence vs clinical trials?
Real-world evidence is evidence collected outside the controlled environment of randomized clinical trials. It helps us to understand disease...
Longer life vs a better death
There has been a lot of debate in recent years about when palliative care should be offered to people?...
Intravenous or Nebulized Magnesium sulfate: Which One Should you Choose?
Magnesium sulfate (MgSO4) has been proposed as an adjunct therapy for severe and potentially fatal asthma exacerbations. If used...
Clarifying the use of thiazide diuretics in Stage 4 chronic kidney disease
Thiazide diuretics, which are used to control hypertension, have been commonly believed to not work well in patients with...
Advancements in clinical trials can pave the way to innovative treatment
Clinical trials and research aim to study new tests and treatments and evaluate the outcome of a study on...
Cervical Cancer: It’s Not Only Preventable But Treatable
Overview Cervical cancer is developed when the cells of the cervix (entrance to the uterus from the vagina) grow...
Wondering about new treatment options for complicated disorders affecting the quality of life?
Complicated disorders may affect the structure and function of all types of organisms. The disorders may affect the patients...
Hurler syndrome gene therapy shows early success in a small study
Hurler syndrome (also called mucopolysaccharidosis type 1, Hurler variant [MPSIH]), is a genetic disorder that causes abnormal musculoskeletal development,...