Rare disease advances: FDA approves three new treatments
Keywords: rare disease, rare disorders, achondroplastic dwarfism Meta Description: In November and December 2021, the FDA approved innovative treatments...
MDforLives
Real-world evidence vs clinical trials?
Real-world evidence is evidence collected outside the controlled environment of randomized clinical trials. It helps us to understand disease...
Longer life vs a better death
There has been a lot of debate in recent years about when palliative care should be offered to people?...
Intravenous or Nebulized Magnesium sulfate: Which One Should you Choose?
Magnesium sulfate (MgSO4) has been proposed as an adjunct therapy for severe and potentially fatal asthma exacerbations. If used...
CRISPR gene editing: In search of perfection
In 2012, Biochemists Jennifer Doudna and Emmanuelle Charpentier made one of the most important discoveries in the history of...
Early-Life Antibiotic Exposure, Gut Microbiome, and Neurodevelopment
Over the past few decades, there has been a dramatic increase in the incidence of childhood neurodevelopmental disorders such...
Avapritinib approved by FDA for use in systemic mastocytosis
On June 16, 2021, the FDA approved a new targeted drug for advanced systemic mastocytosis, a group of rare...
Type 2 diabetes may be a result of inadequate sleep during childhood
Such interesting and important questions have been answered by a new London-based study. Professor Christopher G Owen from St...
Idhifa has been approved for the treatment of relapsed or refractory acute myeloid leukemia
Acute myeloid leukemia (AML) is an aggressive blood and bone marrow cancer where not all leukemic cells are destroyed...
Weekly drinking associated with a reduced risk of diabetes
The effects of alcohol on human health and its association with diseases have long been a matter of research....